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Role Description

Ultragenyx is seeking an experienced physician leader with a passion for rare and ultra-rare diseases. Reporting to the Global Medical Lead, the Director will be a key contributor to shaping the strategy and executing the medical affairs plans for LC-FAOD, MPS VII, and MPS IIIA.

This role offers a unique opportunity to be part of highly collaborative cross-functional teams working on both approved therapies (Dojolvi and Mepsevii) and an investigational AAV gene therapy (UX111) as we prepare for future potential launches.

Work Model: Remote: Officially documented as working full-time from home, with travel to Ultragenyx's offices or other locations on occasion as needed.

Responsibilities:

• Provide strategic medical and scientific leadership to LC‑FAOD (Dojolvi) and the MPS programs (MPS VII and MPS IIIA) to support the development and execution of the global medical plans.
• Contribute to the development and execution of the annual Integrated Evidence Generation Plans.
• Provide medical expertise and leadership to Real-World Evidence initiatives (e.g., ISTs, collaborative research) and the Disease Monitoring Programs for LC‑FAOD and MPS focused on data generation and publication activities.
• Act as a subject matter expert in assigned therapeutic areas, guiding and contributing to the execution of key global medical affairs activities including advisory boards, medical education initiatives, and congress activities.
• Lead robust scientific engagement and education, maintaining strong relationships with external stakeholders to generate insights and advance scientific understanding of assigned programs.
• Provide scientific and medical leadership as needed for publication and medical communication material development.
• Serve as a medical reviewer for promotional materials and non-promotional scientific materials ensuring accuracy, balance, strategic alignment, and compliance with regulatory requirements.
• Provide subject matter expertise to develop and deliver training across the organization.
• Collaborate cross-functionally with Clinical Development, Commercial, Regulatory, HEOR, Biostatistics, Patient Advocacy, Regional Medical Teams, and others to achieve program goals.

Qualifications

• Medical Doctor (MD or DO) required.
• Clinical expertise in the management of patients with inherited metabolic and/or neurodegenerative rare diseases strongly preferred.
• At least 2 years of experience in the pharmaceutical industry is preferred, but extensive relevant clinical experience may be considered as an alternative.
• Strategic thinker with strong execution discipline and a proven ability to manage multiple projects.
• Ability to interpret and communicate complex clinical and scientific information to a range of audiences.
• Highly analytical in approach to work, with the ability to identify interdependencies, consider the medical implications, and understand the broader goals of a program and the organization.
• Ability to work independently and as a member of a cross-functional matrix team in a fast-paced environment.
• High attention to detail, demand for high-quality work, and sense of passion and urgency to achieve goals and improve the lives of patients.
• Willingness and ability to travel up to 15%, including domestic and international engagements.

Benefits

• Generous vacation time and public holidays observed by the company.
• Volunteer days.
• Long term incentive and Employee stock purchase plans or equivalent offerings.
• Employee wellbeing benefits.
• Fitness reimbursement.
• Tuition sponsoring.
• Professional development plans.
• Benefits vary by region and country.